This baby boy was treated with the first personalized gene-editing drug

Doctors successfully treated a baby with a rare genetic disorder using custom-designed gene editing. The treatment, developed in under seven months, used base editing to correct a single DNA letter in the child's CPS1 gene. This marks the first individualized gene-editing therapy. While promising for rare genetic diseases, it highlights challenges in making such personalized treatments widely available due to high costs and limited commercial potential. The case demonstrates both the potential of precision medicine and the need to address accessibility issues for ultra-rare conditions.